Gene therapy could prevent blindness

American regulators have approved a gene therapy that treats an 'inherited form of vision loss'. In a first for gene therapy, the U.S. Food and Drug Administration (FDA) has backed the treatment, developed b...

Blindness cure in sight

(USA) A gene therapy that could treat blindness in people with 'inherited retinal diseases' is on the brink of being approved by regulators in America. Research presented this week to the American Academy...

Gene therapy gives boy his life back

A European medical team has successfully used gene therapy to transform the life of a young boy with serious skin damage. Scientists from Germany's Ruhr-Universität Bochum's burn unit and the Center for Rege...

Gene therapies turn tables on cancer

(USA) This is turning out to be a historic year in the fight against cancer. Pioneering gene therapies approved by American regulators could spell "the end for blood cancer" according to one industry expe...

Experts back life-saving cancer drug

(USA) A game-changing cancer therapy has taken a major step to becoming commercially available after an expert American panel voted unanimously in its favour. By 10 to 0, the US Food and Drug Administrati...

Progress in fight against rare disease

(USA) A leading biosciences company is developing a new gene therapy that shows signs of improving muscle function in patients suffering from a severe form of muscular dystrophy. Solid Biosciences announc...